Total submissions: 8
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000672596 | SCV000797711 | likely pathogenic | Sjögren-Larsson syndrome | 2018-02-07 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV001383429 | SCV001582570 | pathogenic | not provided | 2023-10-14 | criteria provided, single submitter | clinical testing | This sequence change replaces arginine, which is basic and polar, with cysteine, which is neutral and slightly polar, at codon 228 of the ALDH3A2 protein (p.Arg228Cys). This variant is present in population databases (rs72547566, gnomAD 0.003%). This missense change has been observed in individuals with Sjögren–Larsson syndrome (PMID: 10577908, 27717089, 28257279, 28471629, 30925032). It has also been observed to segregate with disease in related individuals. ClinVar contains an entry for this variant (Variation ID: 556574). An algorithm developed to predict the effect of missense changes on protein structure and function (PolyPhen-2) suggests that this variant is likely to be disruptive. Experimental studies have shown that this missense change affects ALDH3A2 function (PMID: 10577908). This variant disrupts the p.Arg228 amino acid residue in ALDH3A2. Other variant(s) that disrupt this residue have been determined to be pathogenic (PMID: 22397046, 29704247). This suggests that this residue is clinically significant, and that variants that disrupt this residue are likely to be disease-causing. For these reasons, this variant has been classified as Pathogenic. |
Gene |
RCV001383429 | SCV002099564 | pathogenic | not provided | 2022-02-24 | criteria provided, single submitter | clinical testing | Published functional studies demonstrate a damaging effect with significant loss of enzyme activity for the R228C mutant at 9% of the wild-type activity (Rizzo et al., 1999); Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 16476818, 10577908, 30925032, 31456290, 16837225, 28257279, 28471629, 25047030, 27717089, 32395410) |
Fulgent Genetics, |
RCV000672596 | SCV002775173 | pathogenic | Sjögren-Larsson syndrome | 2022-01-17 | criteria provided, single submitter | clinical testing | |
ARUP Laboratories, |
RCV000672596 | SCV003799962 | pathogenic | Sjögren-Larsson syndrome | 2022-03-10 | criteria provided, single submitter | clinical testing | |
Al Jalila Children’s Genomics Center, |
RCV000672596 | SCV005420486 | pathogenic | Sjögren-Larsson syndrome | 2024-10-04 | criteria provided, single submitter | research | PS3,PM3,PP1,PM2,PP3,PM5 |
Sharon lab, |
RCV000672596 | SCV001160895 | likely pathogenic | Sjögren-Larsson syndrome | 2019-06-23 | no assertion criteria provided | research | |
Natera, |
RCV000672596 | SCV002093179 | pathogenic | Sjögren-Larsson syndrome | 2017-08-02 | no assertion criteria provided | clinical testing |