Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Kasturba Medical College, |
RCV001806351 | SCV002053877 | pathogenic | Infantile GM1 gangliosidosis | criteria provided, single submitter | clinical testing | ||
Labcorp Genetics |
RCV001869565 | SCV002236340 | pathogenic | Mucopolysaccharidosis, MPS-IV-B; GM1 gangliosidosis | 2023-02-22 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. ClinVar contains an entry for this variant (Variation ID: 1332777). This premature translational stop signal has been observed in individual(s) with GM1 gangliosidosis (PMID: 21497194). This variant is not present in population databases (gnomAD no frequency). This sequence change creates a premature translational stop signal (p.Lys142Serfs*27) in the GLB1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in GLB1 are known to be pathogenic (PMID: 18524657). |