Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV000414223 | SCV000491075 | likely pathogenic | not provided | 2025-02-20 | criteria provided, single submitter | clinical testing | Reported with a second HSD17B4 variant on the opposite allele (in trans) in a patient with progressive spasticity, abnormality of peripheral nerve conduction, and developmental regression in the published literature (PMID: 34440436); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; Not observed at significant frequency in large population cohorts (gnomAD); This variant is associated with the following publications: (PMID: 34440436) |
Eurofins Ntd Llc |
RCV000414223 | SCV000858413 | uncertain significance | not provided | 2017-11-28 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV001314566 | SCV001505102 | uncertain significance | Bifunctional peroxisomal enzyme deficiency; Perrault syndrome | 2022-08-15 | criteria provided, single submitter | clinical testing | This sequence change replaces aspartic acid, which is acidic and polar, with asparagine, which is neutral and polar, at codon 510 of the HSD17B4 protein (p.Asp510Asn). This variant is present in population databases (rs191468413, gnomAD 0.009%). This missense change has been observed in individual(s) with D-bifunctional protein deficiency (PMID: 34440436). ClinVar contains an entry for this variant (Variation ID: 372681). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt HSD17B4 protein function. In summary, the available evidence is currently insufficient to determine the role of this variant in disease. Therefore, it has been classified as a Variant of Uncertain Significance. |