Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000665075 | SCV000789134 | likely pathogenic | Bifunctional peroxisomal enzyme deficiency | 2017-01-11 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV001861740 | SCV002163552 | pathogenic | Bifunctional peroxisomal enzyme deficiency; Perrault syndrome | 2022-07-29 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Phe90Leufs*4) in the HSD17B4 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in HSD17B4 are known to be pathogenic (PMID: 11810648, 16385454). For these reasons, this variant has been classified as Pathogenic. ClinVar contains an entry for this variant (Variation ID: 550351). This variant has not been reported in the literature in individuals affected with HSD17B4-related conditions. This variant is not present in population databases (gnomAD no frequency). |
Baylor Genetics | RCV000665075 | SCV004192405 | likely pathogenic | Bifunctional peroxisomal enzyme deficiency | 2023-11-22 | criteria provided, single submitter | clinical testing | |
Mayo Clinic Laboratories, |
RCV003480748 | SCV004226558 | likely pathogenic | not provided | 2022-06-29 | criteria provided, single submitter | clinical testing | PM2, PVS1 |