Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Molecular Medicine for Neurodegenerative and Neuromuscular Diseases Unit, |
RCV001645023 | SCV001519140 | likely pathogenic | Perrault syndrome 1 | 2021-07-12 | criteria provided, single submitter | research | |
Labcorp Genetics |
RCV002546240 | SCV003439224 | pathogenic | Bifunctional peroxisomal enzyme deficiency; Perrault syndrome | 2024-01-07 | criteria provided, single submitter | clinical testing | This sequence change replaces valine, which is neutral and non-polar, with leucine, which is neutral and non-polar, at codon 218 of the HSD17B4 protein (p.Val218Leu). This variant is not present in population databases (gnomAD no frequency). This missense change has been observed in individuals with D-bifunctional protein deficiency (PMID: 16385454). ClinVar contains an entry for this variant (Variation ID: 1027412). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) has been performed at Invitae for this missense variant, however the output from this modeling did not meet the statistical confidence thresholds required to predict the impact of this variant on HSD17B4 protein function. For these reasons, this variant has been classified as Pathogenic. |
Baylor Genetics | RCV003469556 | SCV004192420 | likely pathogenic | Bifunctional peroxisomal enzyme deficiency | 2024-02-22 | criteria provided, single submitter | clinical testing |