Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV000851627 | SCV005061691 | uncertain significance | Glanzmann thrombasthenia | 2024-05-02 | reviewed by expert panel | curation | The c.1005_1013del variant is predicted to cause a change in the length of the protein due to an in-frame deletion of 4 amino acids and insertion of 1 amino acid in a non-repeat region (p.His335_Leu338delinsGln) (PM4). There has been one case of Glanzmann Thrombasthenia associated with this variant reported in the literature. GT patient TGP0218 (PMID: 31064749) is homozygous for this variant 0.5pt (PM3_supporting). Information about the phenotypes of this patient were insufficient to meet group criteria (PP4 not met). This variant was not present in the GT database or the HGMD database. This variant is absent from gnomAD v4.0.0 (PM2_Supporting). In summary, this variant meets the criteria to be classified as variant of unknown significance due to insufficient evidence for autosomal recessive Glanzmann Thrombasthenia based on the ACMG/AMP criteria applied, as specified by the ClinGen PD VCEP: PM4, PM2_supporting, PM3_supporting. (VCEP specifications version 2; date of approval 05/02/2024) |
NIHR Bioresource Rare Diseases, |
RCV000851627 | SCV000899395 | likely pathogenic | Glanzmann thrombasthenia | 2019-02-01 | criteria provided, single submitter | research |