Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV001254664 | SCV001809904 | likely pathogenic | Glanzmann thrombasthenia | 2022-08-05 | reviewed by expert panel | curation | The NM_000419.5(ITGA2B):c.1361G>A (p.Gly454Asp) variant has been reported, in the homozygous state, in at least one GT proband (P3 in PMID: 34275420) who displayed mucocutaneous bleeding and impaired aggregation with all agonists except ristocetin, which is highly specific for Glanzmann thrombasthenia. Additionally, αIIbβ3 surface expression was reduced to <5%, as measured by flow cytometry (PP4_strong). The variant is absent from population databases, including gnomAD and is predicted deleterious (REVEL score 0.812). In summary, this variant meets criteria to be classified as Likely Pathogenic for GT. GT-specific criteria applied: PM2_supporting, PM3_supporting, PP4_strong and PP3. |
Departement d'Immunology Plaquettaire, |
RCV001254664 | SCV001430683 | pathogenic | Glanzmann thrombasthenia | criteria provided, single submitter | provider interpretation | The variant impairs the expression of the platelets fibrinogen receptor alphaIIb beta3 |