Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV002511514 | SCV002820902 | pathogenic | Glanzmann thrombasthenia | 2022-10-06 | reviewed by expert panel | curation | The NM_000419.5(ITGA2B):c.1591C>T (p.Gln531Ter) nonsense variant in exon 16/30 is predicted to to cause a premature stop codon in a biologically-relevant-exon and is predicted to lead to nonsense mediated decay in a gene in which loss-of-function is an established disease mechanism (PVS1). GT type 1 patient NA (PMID: 11798398) is homozygous for this variant (PM3_supporting). This variant is absent from gnomAD v2.1.1 (PM2_Supporting). In summary, this variant meets the criteria to be classified as Pathogenic for autosomal recessive Glanzmann Thrombasthenia based on the ACMG/AMP criteria applied, as specified by the ClinGen PD VCEP: PVS1, PM2_supporting, PM3_supporting. |