Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV001290504 | SCV001478545 | pathogenic | Glanzmann thrombasthenia | 2020-11-10 | reviewed by expert panel | curation | The NM_000419.4:c.1652G>A (p.Arg551Gln) variant is reported in at least 4 homozygous GT probands in the literature (PMIDs: 26096001, 29675921, 19172520) as well as two additional affected family members (PMID: 26096001). It is found at an extremely low frequency with a MAF of 0.00006536 in the South Asian gnomAD population. And it is predicted damaging by in-silico tools (REVEL score of 0.739). It occurs at the same amino acid residue as Pathogenic variant NM_000419.5:c.1651C>T (p.Arg551Trp). In summary, this variant meets criteria to be classified as Pathogenic for GT. GT-specific criteria applied: PM2_Supporting, PM3, PP1_Moderate, PP3, PP4_Strong, and PM5. |