Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV001254662 | SCV001809921 | pathogenic | Glanzmann thrombasthenia | 2022-06-08 | reviewed by expert panel | curation | The NM_000419.5(ITGA2B):c.240_241del (p.Glu80fs) frameshift variant occurs in exon 2 of 30 where it creates a premature stop codon and is predicted to result in NMD. At least one patient (P1 in PMID: 34275420) is homozygous for this variant (PM3_supporting) and displayed mucocutaneous bleeding and impaired aggregation with all agonists except ristocetin, which is highly specific for Glanzmann thrombasthenia. Additionally, alphaIIbbeta3 surface expression was reduced to <5%, as measured by flow cytometry (PP4_strong). It is absent from gnomAD, ExAC, 1000 Genomes, and ESP. In summary, this variant meets criteria to be classified as pathogenic for GT. GT-specific criteria applied: PP4_Strong, PM2_Supporting, PM3_supporting, and PVS1. |
Departement d'Immunology Plaquettaire, |
RCV001254662 | SCV001430681 | pathogenic | Glanzmann thrombasthenia | criteria provided, single submitter | provider interpretation | The variant alters the expression of the platelets fibrinogen receptor alphaIIb beta3 |