Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV002511559 | SCV002820956 | pathogenic | Glanzmann thrombasthenia | 2022-11-15 | reviewed by expert panel | curation | NM_000419.5(ITGA2B):c.2702C>A (p.Ser901Ter) found in three unrelated homozygous probands from Tunisia (PMID:30325339; PM3) causes a premature stop codon at exon 26 and is predicted to undergo nonsense mediated decay (PVS1). At least one patient with this variant displayed abnormal bleeding and an impaired response to agonists, with a normal response to ristocetin, which is characteristic of Glanzmann thrombasthenia (PMID:30325339; PP4_moderate). The variant was not found in gnomAD v2.1.1 (PM2_supporting). In summary, this variant meets the criteria to be classified as pathogenic for autosomal recessive Glanzmann thrombasthenia based on the ACMG/AMP criteria applied, as specified by the ClinGen PD VCEP: PVS1, PM2_supporting, PP4_moderate, and PM3. |