Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV001803423 | SCV002047574 | pathogenic | Glanzmann thrombasthenia | 2021-06-30 | reviewed by expert panel | curation | The NM_000419.5(ITGA2B):c.432G>A (p.Trp144Ter) nonsense variant creates a premature stop codon in exon 4/30 leading to nonsense mediated decay in a gene in which loss-of-function is an established disease mechanism (PVS1). . At least two probands has been reported with this variant, including GT34 of PMID: 29675921 who meets the criteria for PP4_strong. A second patient in PMID: 30138987 is homozygous for Trp144Ter (PM3_supporting). This variant is absent from gnomAD v2.1.1 (PM2_Supporting). In summary, this variant meets the criteria to be classified as Pathogenic for autosomal recessive Glanzmann Thrombasthenia based on the ACMG/AMP criteria applied, as specified by the ClinGen PD VCEP: PVS1, PM2_supporting, PM3_supporting, PP4_strong. (VCEP specifications version 2; date of approval xx/xx/xxxx) |