Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV001225245 | SCV001397497 | pathogenic | Glanzmann thrombasthenia | 2020-09-06 | reviewed by expert panel | curation | The canonical splice site variant NM_000419.4:c.624+2C>A predicted to affect splicing at intron 5 causing a frameshift and premature stop codon that leads to NMD (confirmed in by RT-PCR in patient cells). This variant is absent from all population databases but has been reported in one compound heterozygous proband with a phenotype highly specific to GT (PMID: 9920835). In summary, this variant meets criteria to be classified as Pathogenic for GT. GT-specific criteria applied: PVS1, PM2_Supporting, and PP4_Moderate. |