Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
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Clin |
RCV001580219 | SCV001809852 | likely pathogenic | Glanzmann thrombasthenia | 2024-09-05 | reviewed by expert panel | curation | The NM_000419.5(ITGA2B):c.647C>T (p.Ala216Val) missense variant has been previously reported in the context of Glanzmann thrombasthenia. One individual (GT55) with the p.Ala216Val missense variant in homozygous state (PM3_supporting) presented with significant mucocutaneous bleeding. Platelet aggregometry demonstrated absence of platelet aggregation with 3 platelet agonists and normal aggregation with ristocetin. Surface expression of αIIbβ3 was demonstrated to be reduced (11-22%) by flowcytometry. Sanger sequencing ensured coverage of exons and splice sites of the ITGA2B and ITGB3 genes as well as untranslated regions (PMID:25728920; PP4_strong). This variant is absent from all continental populations in gnomAD v4.1.0 (PM2_Supporting). Multiple in silico tools predict this variant to be deleterious (REVEL score = 0.85; PP3). This variant meets criteria for PP4_strong, PM2_supporting, PM3_supporting and PP3 and is classified as Likely pathogenic. |