Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Foundation for Research in Genetics and Endocrinology, |
RCV004794465 | SCV000965689 | pathogenic | Muscular dystrophy, limb-girdle, autosomal recessive 23 | 2019-06-24 | criteria provided, single submitter | clinical testing | A heterozygous variant c.4959+1del has been observed in the LAMA2 gene. The proband, born of a consanguineous marriage, presented with clinical indications of large eyes, weakness of all four limbs (proximal>distal), hypotonia, hyperextensible right elbow, contractures of the ankle, knees and left elbow and chronic thrombocytopenia. Her brain MRI showed hyperintense signal changes. The patient in our clinical analysis was observed with the said variant in an autosomal recessive mode of inheritance. The variant has not been reported in the 1000 genomes database and in the ExAC databases. The in-silico prediction of the variant is damaging by MutationTaster2. In summary, the said variant meets our criteria to be classified as likely pathogenic based on the mode of inheritance, in silico prediction. |