Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Clin |
RCV003401396 | SCV004102809 | uncertain significance | Recombinase activating gene 1 deficiency | 2023-11-14 | reviewed by expert panel | curation | The c.527G>T (NM_000448.3) variant in RAG1 is a missense variant predicted to cause a substitution of Cysteine by Phenylalanine at amino acid 176 (p.Cys176Phe). The filtering allele frequency (the upper threshold of the 95% CI of 3/128742) of the c.527G>T variant in RAG1 is 0.000002930 for European (non-Finnish) chromosomes by gnomAD v2.1.1, which is lower than the ClinGen SCID VCEP threshold (<0.000102) for PM2_Supporting, and therefore meets this criterion (PM2_Supporting). This variant has been detected in at least two individuals with SCID and Leaky SCID who are homozygous for the variant (1 pt, PM3; PMID: 28769923 and 34539671). At least one patient with this variant displayed Diagnostic criteria for Leaky SCID (0.5pts) + SCID gene panel (0.5pts) + T-B-NK+ lymphocyte subset profile (0.5 pts), total 1.5 points, PP4 met (PMID: 34539671). In summary, this variant meets the criteria to be classified as Uncertain significance for autosomal recessive SCID based on the ACMG/AMP criteria applied, PM2_Supporting, PM3, and PP4, as specified by the ClinGen SCID VCEP (VCEP specifications version 1). |
Gene |
RCV000413643 | SCV000490762 | likely pathogenic | not provided | 2016-04-29 | criteria provided, single submitter | clinical testing | To our knowledge, the C176F missense variant has neither been published as a pathogenic variant, norreported as a benign polymorphism. C176F represents a non-conservative amino acid substitution as apolar Cysteine residue is replaced with a non-polar Phenylalanine residue; the loss of the Cysteine residuecould also affect normal disulfide bond formation in the protein. In addition, the position in the RAG1protein where this substitution occurs is highly conserved among species. Therefore, C176F is a strongcandidate for a pathogenic variant; however, the possibility that it is a benign variant cannot beexcluded. |
Labcorp Genetics |
RCV000792591 | SCV000931897 | pathogenic | Combined immunodeficiency with skin granulomas; Severe combined immunodeficiency, autosomal recessive, T cell-negative, B cell-negative, NK cell-positive | 2024-09-02 | criteria provided, single submitter | clinical testing | This sequence change replaces cysteine, which is neutral and slightly polar, with phenylalanine, which is neutral and non-polar, at codon 176 of the RAG1 protein (p.Cys176Phe). This variant is present in population databases (rs149229197, gnomAD 0.002%). This missense change has been observed in individual(s) with severe combined immunodeficiency (SCID) and delayed onset combined immunodeficiency with autoimmune/granulomatous manifestations (CID-G/AI) (PMID: 26457731, 28769923; internal data). ClinVar contains an entry for this variant (Variation ID: 372487). Invitae Evidence Modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) has been performed for this missense variant. However, the output from this modeling did not meet the statistical confidence thresholds required to predict the impact of this variant on RAG1 protein function. For these reasons, this variant has been classified as Pathogenic. |
Baylor Genetics | RCV003476000 | SCV004200521 | likely pathogenic | Combined immunodeficiency due to partial RAG1 deficiency | 2023-11-10 | criteria provided, single submitter | clinical testing | |
Fulgent Genetics, |
RCV005044625 | SCV005683451 | likely pathogenic | Combined immunodeficiency due to partial RAG1 deficiency; Combined immunodeficiency with skin granulomas; Histiocytic medullary reticulosis; Severe combined immunodeficiency, autosomal recessive, T cell-negative, B cell-negative, NK cell-positive | 2024-03-26 | criteria provided, single submitter | clinical testing |