Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Leeds Amelogenesis Imperfecta Research Group, |
RCV000240738 | SCV000264807 | pathogenic | Heimler syndrome 1 | 2015-10-01 | criteria provided, single submitter | research | Newly identified |
Labcorp Genetics |
RCV001383603 | SCV001582805 | pathogenic | Zellweger spectrum disorders | 2020-03-17 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. Loss-of-function variants in PEX1 are known to be pathogenic (PMID: 9398847, 16086329, 16141001, 21031596). This variant has been observed in individual(s) with Heimler syndrome (PMID: 27302843). ClinVar contains an entry for this variant (Variation ID: 224324). This variant is not present in population databases (ExAC no frequency). This sequence change creates a premature translational stop signal (p.Thr598Glnfs*11) in the PEX1 gene. It is expected to result in an absent or disrupted protein product. |