Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000666769 | SCV000791119 | uncertain significance | Peroxisome biogenesis disorder 1A (Zellweger) | 2017-05-02 | criteria provided, single submitter | clinical testing | |
Baylor Genetics | RCV001004316 | SCV001163197 | likely pathogenic | Peroxisome biogenesis disorder 1A (Zellweger); Peroxisome biogenesis disorder 1B | criteria provided, single submitter | clinical testing | ||
Labcorp Genetics |
RCV001377622 | SCV001575004 | likely pathogenic | Zellweger spectrum disorders | 2022-11-07 | criteria provided, single submitter | clinical testing | In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as Likely Pathogenic. This variant disrupts the p.Arg1013 amino acid residue in PEX1. Other variant(s) that disrupt this residue have been determined to be pathogenic (PMID: 27124789, 30561787). This suggests that this residue is clinically significant, and that variants that disrupt this residue are likely to be disease-causing. Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt PEX1 protein function. ClinVar contains an entry for this variant (Variation ID: 551650). This missense change has been observed in individuals with Zellweger spectrum disorder (PMID: 16141001, 20952722). This variant is not present in population databases (gnomAD no frequency). This sequence change replaces arginine, which is basic and polar, with histidine, which is basic and polar, at codon 1013 of the PEX1 protein (p.Arg1013His). |
Baylor Genetics | RCV003472081 | SCV004203297 | likely pathogenic | Heimler syndrome 1 | 2023-08-29 | criteria provided, single submitter | clinical testing |