Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000669598 | SCV000794368 | uncertain significance | Infantile hypophosphatasia | 2017-10-07 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV001378584 | SCV001576186 | pathogenic | not provided | 2023-12-17 | criteria provided, single submitter | clinical testing | This sequence change replaces valine, which is neutral and non-polar, with methionine, which is neutral and non-polar, at codon 459 of the ALPL protein (p.Val459Met). This variant is not present in population databases (gnomAD no frequency). This missense change has been observed in individuals with ALPL-related conditions (PMID: 11438998, 27699270, 31707452). ClinVar contains an entry for this variant (Variation ID: 554044). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt ALPL protein function with a positive predictive value of 95%. Experimental studies have shown that this missense change affects ALPL function (PMID: 31707452). This variant disrupts the p.Val459 amino acid residue in ALPL. Other variant(s) that disrupt this residue have been observed in individuals with ALPL-related conditions (PMID: 19500388, 29724887), which suggests that this may be a clinically significant amino acid residue. For these reasons, this variant has been classified as Pathogenic. |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV004586861 | SCV005077062 | pathogenic | Hypophosphatasia | 2024-04-22 | criteria provided, single submitter | clinical testing | Variant summary: ALPL c.1375G>A (p.Val459Met) results in a conservative amino acid change in the encoded protein sequence. Four of five in-silico tools predict a damaging effect of the variant on protein function. The variant was absent in 244600 control chromosomes. c.1375G>A has been reported in the literature in individuals affected with Hypophosphatasia, either at a compound heterozygous state along with a second pathogenic variant, or at a single heterozygous state (example, DelAngel_2020, Michigami_2020, Sankaran_2020, Taillandier_2001). These data indicate that the variant is likely to be associated with disease. At least one publication reports experimental evidence evaluating an impact on protein function. The most pronounced variant effect results in <10% of normal activity in COS7 cells (Michigami_2020). The following publications have been ascertained in the context of this evaluation (PMID: 32160374, 31707452, 32309015, 11438998). ClinVar contains an entry for this variant (Variation ID: 554044). Based on the evidence outlined above, the variant was classified as pathogenic. |