Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
JKU Lab, |
RCV005215812 | SCV005702154 | likely pathogenic | Hypophosphatasia | 2024-12-10 | criteria provided, single submitter | curation | This missense variant is not present in GnomAD 4.1 and affects a moderately conserved amino acid. The variant is predicted to affect protein function (REVEL score: 0.925). Splice-prediction algorithms predict no effect on splicing. In vitro functional studies showed reduced ALP activity without dominant negative effect. The results of the functional testing and the applied ACMG criteria can be viewed at: https://alplmutationdatabase.jku.at/table/ |