Total submissions: 7
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Invitae | RCV001042961 | SCV001206670 | pathogenic | not provided | 2024-01-29 | criteria provided, single submitter | clinical testing | This sequence change replaces alanine, which is neutral and non-polar, with valine, which is neutral and non-polar, at codon 33 of the ALPL protein (p.Ala33Val). This variant is present in population databases (rs121918005, gnomAD 0.005%). This missense change has been observed in individual(s) with hypophosphatasia (PMID: 1409720, 15694177, 17253930, 22397652, 25731960). ClinVar contains an entry for this variant (Variation ID: 13667). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt ALPL protein function with a positive predictive value of 95%. Experimental studies have shown that this missense change affects ALPL function (PMID: 15694177). For these reasons, this variant has been classified as Pathogenic. |
Baylor Genetics | RCV000014655 | SCV003841204 | pathogenic | Infantile hypophosphatasia | criteria provided, single submitter | clinical testing | ||
Baylor Genetics | RCV003473099 | SCV004194986 | pathogenic | Adult hypophosphatasia | 2023-07-14 | criteria provided, single submitter | clinical testing | |
Laboratory for Molecular Medicine, |
RCV003473099 | SCV004848783 | likely pathogenic | Adult hypophosphatasia | 2022-11-03 | criteria provided, single submitter | clinical testing | The p.Ala33Val variant in ALPL (also referred to in the literature as Ala16Val) has been reported in 6 individuals with hypophosphatasia (Henthorn 1992 PMID: 1409720, Brun-Heath 2005 PMID: 15694177, Whyte 2015 PMID: 25731960, Reis 2021 PMID: 34033304, Zhang 2021 PMID: 34712267). It has also been identified in 0.02% (1/5184) of East Asian chromosomes by gnomAD (http://gnomad.broadinstitute.org) and reported in ClinVar (Variation ID 13667). Computational prediction tools and conservation analyses suggest that this variant may impact the protein, though this information is not predictive enough to determine pathogenicity. In vitro functional studies provide some evidence that this variant results in reduced protein activity compared to wild type (Brun-Heath 2005 PMID: 15694177, Del Angel 2020 PMID: 32160374); however, these types of assays may not accurately represent biological function. In summary, although additional studies are required to fully establish its clinical significance, this variant meets criteria to be classified as likely pathogenic for autosomal recessive hypophosphatasia. ACMG/AMP Criteria applied: PM3_Strong, PS3_Moderate, PP3, PM2_Supporting. |
OMIM | RCV000014655 | SCV000034910 | pathogenic | Infantile hypophosphatasia | 1992-10-15 | no assertion criteria provided | literature only | |
Natera, |
RCV001273156 | SCV001455761 | pathogenic | Hypophosphatasia | 2020-09-16 | no assertion criteria provided | clinical testing | |
Baylor Genetics | RCV001333468 | SCV001526050 | uncertain significance | Childhood hypophosphatasia | 2018-08-08 | flagged submission | clinical testing | This variant was determined to be of uncertain significance according to ACMG Guidelines, 2015 [PMID:25741868]. |