Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000672049 | SCV000797108 | uncertain significance | Metachromatic leukodystrophy | 2018-01-12 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000672049 | SCV001225560 | pathogenic | Metachromatic leukodystrophy | 2023-09-29 | criteria provided, single submitter | clinical testing | This sequence change replaces histidine, which is basic and polar, with tyrosine, which is neutral and polar, at codon 399 of the ARSA protein (p.His399Tyr). This variant is present in population databases (rs199476376, gnomAD 0.0009%). This missense change has been observed in individual(s) with metachromatic leukodystrophy (MLD) (PMID: 9452102, 20339381, 28762252). This variant is also known as 1189C>T or H397Y. ClinVar contains an entry for this variant (Variation ID: 68117). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt ARSA protein function. Experimental studies have shown that this missense change affects ARSA function (PMID: 9452102, 28762252). For these reasons, this variant has been classified as Pathogenic. |
Uni |
RCV000058947 | SCV000090468 | not provided | not provided | no assertion provided | not provided | ||
Gelb Laboratory, |
RCV000672049 | SCV005046769 | not provided | Metachromatic leukodystrophy | no assertion provided | in vitro |