Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Foundation for Research in Genetics and Endocrinology, |
RCV003318425 | SCV004021943 | pathogenic | Metachromatic leukodystrophy | 2023-07-27 | criteria provided, single submitter | clinical testing | A Homozygous variation in exon 2 of the ARSA gene that results in the amino acid substitution of Threonine for Lysine at codon 125 was detected. The observed variant c.374A>C (p.Lys125Thr) has not been reported in the 1000 genomes and gnomAD databases. The in silico prediction of the variant is disease causing by MutationTaster, SIFT, PolyPhen-2, CADD and DANN. In summary, the variant meets our criteria to be classified as pathogenic. |