Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Molecular Genetics Laboratory, |
RCV004787561 | SCV005402673 | likely pathogenic | Alpha thalassemia-X-linked intellectual disability syndrome | 2024-11-20 | criteria provided, single submitter | clinical testing | This variant was detected in a male with severe intellectual disability and renal hypoplasia. This variant in the X-linked gene was confirmed to be inherited from unaffected mother and was found in his healthy sister as well. Rare missense variants affecting the ATRX gene are well documented as a molecular cause of "X-linked alpha-thalassemia/impaired intellectual development syndrome" (OMIM:301040) (PMID:16813605;1770528;7726225;11449489). To conclude, the variant is classified as likely pathogenic (ACMG PM2, PM1, PP3, PP2). |