Total submissions: 6
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000047247 | SCV000220603 | likely pathogenic | Cystic fibrosis | 2014-08-20 | criteria provided, single submitter | literature only | |
Labcorp Genetics |
RCV000047247 | SCV001590398 | pathogenic | Cystic fibrosis | 2023-07-10 | criteria provided, single submitter | clinical testing | This sequence change affects a donor splice site in intron 6 of the CFTR gene. It is expected to disrupt RNA splicing. Variants that disrupt the donor or acceptor splice site typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in CFTR are known to be pathogenic (PMID: 1695717, 7691345, 9725922). This variant is not present in population databases (gnomAD no frequency). Disruption of this splice site has been observed in individuals with cystic fibrosis (PMID: 7472820, 12454843, 19481507, 22658665). This variant is also known as c.875+1G>C. ClinVar contains an entry for this variant (Variation ID: 54052). Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site. For these reasons, this variant has been classified as Pathogenic. |
Mayo Clinic Laboratories, |
RCV001509316 | SCV001715950 | likely pathogenic | not provided | 2019-05-01 | criteria provided, single submitter | clinical testing | PVS1, PM2 |
Baylor Genetics | RCV003474617 | SCV004213359 | pathogenic | Bronchiectasis with or without elevated sweat chloride 1 | 2023-09-26 | criteria provided, single submitter | clinical testing | |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV000047247 | SCV005380388 | likely pathogenic | Cystic fibrosis | 2024-08-22 | criteria provided, single submitter | clinical testing | Variant summary: CFTR c.743+1G>C is located in a canonical splice-site and is predicted to affect mRNA splicing resulting in a significantly altered protein due to either exon skipping, shortening, or inclusion of intronic material. Variants that disrupt the consensus splice site are a relatively common cause of aberrant splicing and loss of CFTR function. Several computational tools predict a significant impact on normal splicing: Three predict the variant abolishes a 5' splicing donor site. However, these predictions have yet to be confirmed by functional studies. The variant was absent in 251316 control chromosomes. c.743+1G>C, also known under the legacy name 875+1G>C, has been reported in the literature in individuals affected with Cystic Fibrosis (e.g., Wilschanski_1995, Scotet_2003). These data indicate that the variant is likely to be associated with disease. To our knowledge, no experimental evidence demonstrating an impact on protein function has been reported. The following publications have been ascertained in the context of this evaluation (PMID: 12815607, 7472820). ClinVar contains an entry for this variant (Variation ID: 54052). Based on the evidence outlined above, the variant was classified as likely pathogenic. |
Natera, |
RCV001831802 | SCV002078134 | pathogenic | CFTR-related disorder | 2017-03-17 | no assertion criteria provided | clinical testing |