Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Laboratory of Diagnosis and Therapy of Lysosomal Disorders, |
RCV001578435 | SCV001547978 | uncertain significance | Mucopolysaccharidosis, MPS-IV-A | 2021-02-01 | criteria provided, single submitter | curation | Absent from gnomAD v2.1.1 (PM2_moderate) |
Neuberg Centre For Genomic Medicine, |
RCV001578435 | SCV005073883 | uncertain significance | Mucopolysaccharidosis, MPS-IV-A | criteria provided, single submitter | clinical testing | The observed splice region, intron variant c.1482+5G>A in GALNS gene has been reported previously in compound heterozygous state in two families with Morquio (Morquio-Brailsford) syndrome (Jezela-Stanek A, et al., 2019). The c.1482+5G>A variant is absent in gnomAD Exomes. This variant has been reported to the ClinVar database as Uncertain Significance. However study on multiple affected individuals and functional studies on the pathogenicity of the variant is unavailable. This variant is predicted to be Likely damaging by SpliceAI Prediction. For these reasons, this variant has been classified as Uncertain Significance. |