Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Foundation for Research in Genetics and Endocrinology, |
RCV003318423 | SCV004021939 | pathogenic | Mucopolysaccharidosis, MPS-IV-A | 2023-07-27 | criteria provided, single submitter | clinical testing | A heterozygous variation in exon 2 of the GALNS gene that results in the amino acid substitution of Proline for Alanine at codon 63 was detected. The observed variant c.187G>C (p.Ala63Pro) has not been reported in the 1000 genomes database. The in silico prediction of the variant is disease causing by PolyPhen-2, SIFT, DANN and MutationTaster. In summary, the variant meets our criteria to be classified as pathogenic. |