Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Foundation for Research in Genetics and Endocrinology, |
RCV002291514 | SCV002583289 | pathogenic | Mucopolysaccharidosis, MPS-IV-A | 2022-07-30 | criteria provided, single submitter | clinical testing | A homozygous single base pair deletion in exon 4 of the GALNS gene (chr16:g. 88841040 del; Depth: 121x) that results in a frameshift and premature truncation of the protein 4 amino acids downstream to codon 125 (p.Pro125ArgfsTer4; ENST00000268695.10) was detected (Table). This variant has not been reported in the 1000 genomes and gnomAD databases and has a minor allele frequency of 0.001% in our internal database. The in silico prediction of the variant is damaging MutationTaster2. The reference region is conserved across species. |