Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Ce |
RCV002211374 | SCV002498200 | likely pathogenic | not provided | 2022-01-01 | criteria provided, single submitter | clinical testing | |
Women's Health and Genetics/Laboratory Corporation of America, |
RCV003994411 | SCV004803238 | uncertain significance | not specified | 2024-02-16 | criteria provided, single submitter | clinical testing | Variant summary: GALNS c.775C>T (p.Arg259Trp) results in a non-conservative amino acid change located in the Sulfatase, N-terminal (IPR000917) of the encoded protein sequence. Five of five in-silico tools predict a damaging effect of the variant on protein function. The variant allele was found at a frequency of 8e-06 in 250168 control chromosomes. c.775C>T has been reported in the literature in at-least three unrelated individuals affected with Mucopolysaccharidosis Type IVA (Morquio Syndrome A), in each case, this variant was seen along with a different apparently pathogenic variant (example, Lv_2021, Moosa_2022, Yi_2022). These data indicate that the variant may be associated with disease. To our knowledge, no experimental evidence demonstrating an impact on protein function has been reported. The following publications have been ascertained in the context of this evaluation (PMID: 34557487, 35616356, 35212421). ClinVar contains an entry for this variant (Variation ID: 1675645). Based on the evidence outlined above, the variant was classified as VUS-possibly pathogenic. |
Gene |
RCV002211374 | SCV005331928 | pathogenic | not provided | 2023-08-10 | criteria provided, single submitter | clinical testing | Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; This variant is associated with the following publications: (PMID: 35212421, 34557487, 35616356) |
Fulgent Genetics, |
RCV005008479 | SCV005641485 | likely pathogenic | Mucopolysaccharidosis, MPS-IV-A | 2024-03-23 | criteria provided, single submitter | clinical testing | |
Genetics and Genomic Medicine Centre, |
RCV005008479 | SCV005873750 | pathogenic | Mucopolysaccharidosis, MPS-IV-A | 2021-05-31 | criteria provided, single submitter | clinical testing |