Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Foundation for Research in Genetics and Endocrinology, |
RCV001093708 | SCV001190356 | likely pathogenic | Mucopolysaccharidosis, MPS-IV-A | criteria provided, single submitter | clinical testing | A compound heterozygous deletion variation in exon 8 of the GALNS gene that results in the premature termination of the protein at codon 280 was detected. The observed variant c.839_841delACA (p.Asn280del) has not been reported in the 1000 genomes, gnomAD and ExAC databases. The in silico prediction of the variant is damaging by MutationTaster2. The reference codon is conserved across species. In summary, the variant meets our criteria to be classified as likely pathogenic. | |
Laboratory of Diagnosis and Therapy of Lysosomal Disorders, |
RCV001093708 | SCV001547804 | uncertain significance | Mucopolysaccharidosis, MPS-IV-A | 2021-02-01 | criteria provided, single submitter | research | Absent from gnomAD v2.1.1 (PM2_moderate); protein length changes as a result of in-frame deletions in a nonrepeat region (PM4_supporting) |