Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Ce |
RCV003887529 | SCV004703755 | pathogenic | not provided | 2024-02-01 | criteria provided, single submitter | clinical testing | HEXA: PVS1, PM2 |
Labcorp Genetics |
RCV005101470 | SCV005744193 | pathogenic | Tay-Sachs disease | 2024-09-07 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Gln350*) in the HEXA gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in HEXA are known to be pathogenic (PMID: 1833974, 8490625). This variant is not present in population databases (gnomAD no frequency). This variant has not been reported in the literature in individuals affected with HEXA-related conditions. Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may create or strengthen a splice site. For these reasons, this variant has been classified as Pathogenic. |