Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000669356 | SCV000794102 | likely pathogenic | Tay-Sachs disease | 2017-09-13 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000669356 | SCV002204868 | pathogenic | Tay-Sachs disease | 2024-09-16 | criteria provided, single submitter | clinical testing | This sequence change creates a premature translational stop signal (p.Gln47*) in the HEXA gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in HEXA are known to be pathogenic (PMID: 1833974, 8490625). This variant is present in population databases (rs745996955, gnomAD 0.007%). This premature translational stop signal has been observed in individual(s) with Tay-Sachs disease (PMID: 12180151). ClinVar contains an entry for this variant (Variation ID: 553832). For these reasons, this variant has been classified as Pathogenic. |