Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
LDLR- |
RCV000238460 | SCV000295236 | likely pathogenic | Hypercholesterolemia, familial, 1 | 2016-03-25 | criteria provided, single submitter | literature only | |
Gene |
RCV004772884 | SCV005384229 | pathogenic | not provided | 2024-04-25 | criteria provided, single submitter | clinical testing | Identified in the heterozygous state in individuals with elevated LDL and total cholesterol and in the compound heterozygous state with a second LDLR variant in individuals with more severe disease in published literature (PMID: 24722143, 29693183); Published functional studies demonstrate a damaging effect: impairs LDL binding and internalization (PMID: 24722143, 29693183); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; Not observed at significant frequency in large population cohorts (gnomAD); Also known as c.28893T>G p.(Cys377Gly) and c.1129T>G p.(Cys356Gly); This variant is associated with the following publications: (PMID: 24722143, 29693183, 27830735, 12459547, 2988123) |