Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Centre de Génétique Moléculaire et Chromosomique, |
RCV000417229 | SCV000503478 | pathogenic | Hypercholesterolemia, familial, 1 | 2016-12-16 | criteria provided, single submitter | clinical testing | subjects mutated among 2600 FH index cases screened = 2 |
Labcorp Genetics |
RCV001851013 | SCV002125582 | pathogenic | Familial hypercholesterolemia | 2021-06-09 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. This variant has been observed in individual(s) with autosomal dominant hypercholesterolemia (PMID: 26802169). ClinVar contains an entry for this variant (Variation ID: 375837). This variant is not present in population databases (ExAC no frequency). This sequence change creates a premature translational stop signal (p.Thr766Serfs*13) in the LDLR gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in LDLR are known to be pathogenic (PMID: 20809525, 28645073). |