Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
LDLR- |
RCV000237550 | SCV000294576 | likely pathogenic | Hypercholesterolemia, familial, 1 | 2016-03-25 | criteria provided, single submitter | literature only | |
Arcensus | RCV000237550 | SCV002564608 | pathogenic | Hypercholesterolemia, familial, 1 | 2013-02-01 | criteria provided, single submitter | clinical testing | |
Ambry Genetics | RCV002436070 | SCV002751749 | pathogenic | Cardiovascular phenotype | 2023-03-20 | criteria provided, single submitter | clinical testing | The c.283T>C (p.C95R) alteration is located in exon 3 (coding exon 3) of the LDLR gene. This alteration results from a T to C substitution at nucleotide position 283, causing the cysteine (C) at amino acid position 95 to be replaced by an arginine (R). This variant was not reported in population-based cohorts in the Genome Aggregation Database (gnomAD). Pathogenic LDLR mutations that result in the substitution or generation of cysteine residues within the cysteine-rich LDLR class A repeats and EGF-like domains are common in familial hypercholesterolemia (FH) (Villéger, 2002). This particular cysteine alteration (also referred to as p.C74R) has been detected in several individuals with FH (Deiana, 2000; Fouchier, 2005; Blesa, 2006; Vandrovcova, 2013). A different variant affecting this codon (p.C95F, c.284G>T) has also been reported in association with FH (Miyake, 2009). Internal structural analysis indicates this alteration eliminates a disulfide bond critical for the structural integrity of LDLR class A repeat 2 (Ambry internal data). This alteration is predicted to be deleterious by in silico analysis. Based on the available evidence, this alteration is classified as pathogenic. |
Laboratorium voor Moleculaire Diagnostiek Experimentele Vasculaire Geneeskunde, |
RCV000237550 | SCV000606061 | pathogenic | Hypercholesterolemia, familial, 1 | no assertion criteria provided | research |