Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
LDLR- |
RCV000238345 | SCV000294692 | pathogenic | Hypercholesterolemia, familial, 1 | 2016-03-25 | criteria provided, single submitter | literature only | |
Labcorp Genetics |
RCV002229687 | SCV000627037 | pathogenic | Familial hypercholesterolemia | 2022-05-20 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. ClinVar contains an entry for this variant (Variation ID: 251208). This premature translational stop signal has been observed in individual(s) with familial hypercholesterolemia (PMID: 22881376, 32331935). This variant is present in population databases (rs755799528, gnomAD 0.006%). This sequence change creates a premature translational stop signal (p.Ser138*) in the LDLR gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in LDLR are known to be pathogenic (PMID: 20809525, 28645073). |
Laboratory for Molecular Medicine, |
RCV004017542 | SCV004847684 | likely pathogenic | Homozygous familial hypercholesterolemia | 2019-04-16 | criteria provided, single submitter | clinical testing | The p.Ser138X variant in LDLR has been reported in one individual with familial hypercholesterolemia (FH; Usifo 2012). It has also been reported by other clinical laboratories in ClinVar (Variation ID: 251208) and has been identified in 0.007% (2/30616) of South Asian chromosomes by gnomAD (http://gnomad.broadinstitute.org). This frequency is low enough to be consistent with the frequency of FH in the general population. This nonsense variant leads to a premature termination codon at position 138, which is predicted to lead to a truncated or absent protein. Loss of function of the LDLR gene is an established disease mechanism in autosomal dominant FH. In summary, although additional studies are required to fully establish its clinical significance, this variant meets criteria to be classified as likely pathogenic for autosomal dominant FH. ACMG/AMP Criteria applied: PVS1, PM2. |