Total submissions: 2
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
LDLR- |
RCV000237205 | SCV000294934 | pathogenic | Hypercholesterolemia, familial, 1 | 2016-03-25 | criteria provided, single submitter | literature only | |
Ambry Genetics | RCV004639190 | SCV005135995 | pathogenic | Cardiovascular phenotype | 2024-05-15 | criteria provided, single submitter | clinical testing | The c.705dupC pathogenic mutation, located in coding exon 5 of the LDLR gene, results from a duplication of C at nucleotide position 705, causing a translational frameshift with a predicted alternate stop codon (p.C236Lfs*4). This variant (also referred to as 'ins C after nt C704') has been detected in individuals with features consistent with familial hypercholesterolemia (Tosi I et al. Atherosclerosis, 2007 Sep;194:102-11; Ambry internal data). This alteration is expected to result in loss of function by premature protein truncation or nonsense-mediated mRNA decay. As such, this alteration is interpreted as a disease-causing mutation. |