Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV000812847 | SCV000953175 | pathogenic | Charcot-Marie-Tooth disease, type I | 2020-12-16 | criteria provided, single submitter | clinical testing | This variant has been reported in several individuals affected with Charcot-Marie-Tooth disease, type 1 (PMID: 9888385, 10093067, 26310628) and has been observed to segregate with Charcot-Marie-Tooth disease in a family (PMID: 11080236 ). For these reasons, this variant has been classified as Pathogenic. Experimental studies have shown that this missense change causes retention of the MPZ protein in the endoplasmic reticulum leading to increased protein degradation (PMID: 29687021). This variant is not present in population databases (ExAC no frequency). This sequence change replaces isoleucine with threonine at codon 99 of the MPZ protein (p.Ile99Thr). The isoleucine residue is highly conserved and there is a moderate physicochemical difference between isoleucine and threonine. |
Molecular Genetics Laboratory, |
RCV000789473 | SCV001336805 | pathogenic | Charcot-Marie-Tooth disease | criteria provided, single submitter | clinical testing | ||
Inherited Neuropathy Consortium | RCV000789473 | SCV000928829 | uncertain significance | Charcot-Marie-Tooth disease | no assertion criteria provided | literature only |