Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Molecular Diagnostics Lab, |
RCV004595808 | SCV005088511 | likely pathogenic | Pelizaeus-Merzbacher disease | 2021-02-19 | criteria provided, single submitter | clinical testing | This missense variant (c.137T>C, p.Leu46Pro) has not been observed in population databases (gnomAD). It has been described in the literature (PMID 9934976, PMID 15712223). Variant prediction programs suggest a deleterious effect on the PLP1 protein, but no functional studies have been published. |