Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Baylor Genetics | RCV000680072 | SCV000807512 | pathogenic | Pelizaeus-Merzbacher disease | 2017-09-01 | criteria provided, single submitter | clinical testing | This nonsense variant is categorized as deleterious according to ACMG guidelines (PMID:18414213) and was found once in our laboratory de novo in a 4-year-old male with global delays, central hypotonia, peripheral spasticity, dysmorphisms, nystagmus, strabisumus, intention tremor |