Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Molecular Diagnostics Lab, |
RCV004595767 | SCV005088446 | likely pathogenic | Pelizaeus-Merzbacher disease | 2021-11-16 | criteria provided, single submitter | clinical testing | This variant (c.359delG, p.Gly120Alafs*27) occurs in a homopolymer region and results in a frameshift to a premature termination. It has not been observed in population databases (gnomAD), nor is it described in the literature. No functional studies have been published. |