Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Molecular Diagnostics Lab, |
RCV004588586 | SCV005077958 | pathogenic | Pelizaeus-Merzbacher disease | criteria provided, single submitter | clinical testing | This variant (c.380_392del, p.Arg127Lys*16) results in a frameshift to a premature termination. It has not been observed in population databases (gnomAD). The change has been reported in the literature (PMID 26125040) but no functional studies have been published. It has been observed in two affected male siblings and is carried by their mother. |