Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Molecular Diagnostics Lab, |
RCV004588588 | SCV005077963 | likely pathogenic | Pelizaeus-Merzbacher disease | criteria provided, single submitter | clinical testing | This variant (c.554_564del, p.Gln185Leufs*15) predicts a frameshift and a premature termination. It has not been observed in population databases (gnomAD). The change has been described in the literature (PMID 21679497) but no functional studies have been published. |