Total submissions: 1
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Molecular Diagnostics Lab, |
RCV004595795 | SCV005088493 | pathogenic | Pelizaeus-Merzbacher disease | 2022-01-24 | criteria provided, single submitter | clinical testing | This intronic variant (c.697-2A>C) has not been observed in population databases (gnomAD) and has not been described in the literature. Splice prediction programs indicate a deleterious effect on normal splicing. |