Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Prevention |
RCV000721257 | SCV000852277 | uncertain significance | not provided | 2016-07-18 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV000820328 | SCV000961036 | pathogenic | RYR1-related disorder | 2024-01-31 | criteria provided, single submitter | clinical testing | This sequence change replaces alanine, which is neutral and non-polar, with threonine, which is neutral and polar, at codon 400 of the RYR1 protein (p.Ala400Thr). This variant is present in population databases (rs777016690, gnomAD 0.003%). This missense change has been observed in individual(s) with clinical features of autosomal recessive RYR1-related myopathy and/or myopathy (PMID: 1069529; Invitae). In at least one individual the data is consistent with being in trans (on the opposite chromosome) from a pathogenic variant. ClinVar contains an entry for this variant (Variation ID: 590393). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) has been performed at Invitae for this missense variant, however the output from this modeling did not meet the statistical confidence thresholds required to predict the impact of this variant on RYR1 protein function. For these reasons, this variant has been classified as Pathogenic. |
Gene |
RCV000721257 | SCV002549243 | likely pathogenic | not provided | 2023-01-17 | criteria provided, single submitter | clinical testing | Not observed at significant frequency in large population cohorts (gnomAD); In silico analysis supports that this missense variant has a deleterious effect on protein structure/function; Identified in a patient with myopathy in published literature (PMID: 31069529); This variant is associated with the following publications: (PMID: 31069529) |
All of Us Research Program, |
RCV004807114 | SCV005430475 | uncertain significance | Malignant hyperthermia, susceptibility to, 1 | 2024-02-22 | criteria provided, single submitter | clinical testing | This missense variant replaces alanine with threonine at codon 400 of the RYR1 protein. Computational prediction suggests that this variant may have deleterious impact on protein structure and function (internally defined REVEL score threshold >= 0.7, PMID: 27666373). To our knowledge, functional studies have not been reported for this variant. This variant has not been reported in individuals affected with autosomal dominant malignant hyperthermia in the literature, although it is associated with other phenotype(s) (ClinVar variation ID: 590393). This variant has been identified in 1/251420 chromosomes in the general population by the Genome Aggregation Database (gnomAD). Due to insufficient evidence, this variant is classified as a Variant of Uncertain Significance for autosomal dominant malignant hyperthermia. |
Fulgent Genetics, |
RCV005027887 | SCV005647451 | likely pathogenic | Central core myopathy; Malignant hyperthermia, susceptibility to, 1; Congenital multicore myopathy with external ophthalmoplegia; King Denborough syndrome | 2024-05-29 | criteria provided, single submitter | clinical testing |