Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Fulgent Genetics, |
RCV002489200 | SCV002776854 | likely pathogenic | Central core myopathy; Malignant hyperthermia, susceptibility to, 1; Congenital multicore myopathy with external ophthalmoplegia; Congenital myopathy with fiber type disproportion; King Denborough syndrome | 2021-08-27 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV003757181 | SCV004553366 | likely pathogenic | RYR1-related disorder | 2025-01-10 | criteria provided, single submitter | clinical testing | This sequence change affects a donor splice site in intron 28 of the RYR1 gene. It is expected to disrupt RNA splicing. Variants that disrupt the donor or acceptor splice site typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in RYR1 are known to be pathogenic (PMID: 23919265, 25960145, 28818389, 30611313). This variant is not present in population databases (gnomAD no frequency). This variant has not been reported in the literature in individuals affected with RYR1-related conditions. ClinVar contains an entry for this variant (Variation ID: 427768). Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site. In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as Likely Pathogenic. |
Gene |
RCV004722827 | SCV005334502 | likely pathogenic | not provided | 2023-11-07 | criteria provided, single submitter | clinical testing | Canonical splice site variant predicted to result in a null allele in a gene for which loss of function is a known mechanism of disease; Not observed at significant frequency in large population cohorts (gnomAD); Has not been previously published as pathogenic or benign to our knowledge |
All of Us Research Program, |
RCV004806371 | SCV005430981 | uncertain significance | Malignant hyperthermia, susceptibility to, 1 | 2024-09-23 | criteria provided, single submitter | clinical testing | |
Institute of Human Genetics, |
RCV000490681 | SCV000579356 | likely pathogenic | Hypotonia | no assertion criteria provided | clinical testing |