Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Gene |
RCV000442837 | SCV000536646 | likely pathogenic | not provided | 2017-02-01 | criteria provided, single submitter | clinical testing | The c.7835+1G>A variant in the RYR1 gene has not been reported previously as a pathogenic variant nor as a benign variant, to our knowledge. This splice site variant destroys the canonical splice donor site in intron 48. It is predicted to cause abnormal gene splicing, either leading to an abnormal message that is subject to nonsense-mediated mRNA decay, or to an abnormal protein product if the message is used for protein translation. The c.7835+1G>A variant was not observed in approximately 6,500 individuals of European and African American ancestry in the NHLBI Exome Sequencing Project, indicating it is not a common benign variant in these populations. We interpret c.7835+1G>A as a likely pathogenic variant. |
Labcorp Genetics |
RCV001865407 | SCV002265954 | likely pathogenic | RYR1-related disorder | 2021-08-18 | criteria provided, single submitter | clinical testing | This sequence change affects a donor splice site in intron 48 of the RYR1 gene. It is expected to disrupt RNA splicing. Variants that disrupt the donor or acceptor splice site typically lead to a loss of protein function (PMID: 16199547), and loss-of-function variants in RYR1 are known to be pathogenic (PMID: 20583297, 20839240, 23919265, 28818389). This variant is not present in population databases (ExAC no frequency). Disruption of this splice site has been observed in individual(s) with RYR1-related conditions (Invitae). ClinVar contains an entry for this variant (Variation ID: 393262). Algorithms developed to predict the effect of sequence changes on RNA splicing suggest that this variant may disrupt the consensus splice site. In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as Likely Pathogenic. |
Fulgent Genetics, |
RCV002488988 | SCV002793416 | likely pathogenic | Central core myopathy; Malignant hyperthermia, susceptibility to, 1; Congenital multicore myopathy with external ophthalmoplegia; Congenital myopathy with fiber type disproportion; King Denborough syndrome | 2021-12-07 | criteria provided, single submitter | clinical testing |