Total submissions: 5
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Prevention |
RCV000721762 | SCV000852897 | uncertain significance | not provided | 2017-09-11 | criteria provided, single submitter | clinical testing | |
Invitae | RCV001312367 | SCV001502816 | likely pathogenic | RYR1-related disorder | 2023-10-27 | criteria provided, single submitter | clinical testing | This sequence change replaces alanine, which is neutral and non-polar, with threonine, which is neutral and polar, at codon 3298 of the RYR1 protein (p.Ala3298Thr). This variant is present in population databases (rs544339193, gnomAD 0.05%). This missense change has been observed in individuals with autosomal recessive congenital myopathy (PMID: 28818389, 30611313; Invitae). It has also been observed to segregate with disease in related individuals. ClinVar contains an entry for this variant (Variation ID: 590640). Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is not expected to disrupt RYR1 protein function with a negative predictive value of 95%. In summary, the currently available evidence indicates that the variant is pathogenic, but additional data are needed to prove that conclusively. Therefore, this variant has been classified as Likely Pathogenic. |
Fulgent Genetics, |
RCV002485830 | SCV002787777 | uncertain significance | Central core myopathy; Malignant hyperthermia, susceptibility to, 1; Congenital multicore myopathy with external ophthalmoplegia; Congenital myopathy with fiber type disproportion; King Denborough syndrome | 2021-11-22 | criteria provided, single submitter | clinical testing | |
Revvity Omics, |
RCV000721762 | SCV003810559 | uncertain significance | not provided | 2023-10-09 | criteria provided, single submitter | clinical testing | |
Muscle and Diseases Team, |
RCV004586902 | SCV005038486 | likely pathogenic | Centronuclear myopathy | 2024-03-01 | criteria provided, single submitter | research | PM2+PM3+PP1+PP2 |