Total submissions: 3
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Labcorp Genetics |
RCV001379382 | SCV001577176 | pathogenic | Niemann-Pick disease, type B; Niemann-Pick disease, type A | 2022-10-11 | criteria provided, single submitter | clinical testing | Advanced modeling of protein sequence and biophysical properties (such as structural, functional, and spatial information, amino acid conservation, physicochemical variation, residue mobility, and thermodynamic stability) performed at Invitae indicates that this missense variant is expected to disrupt SMPD1 protein function. Experimental studies have shown that this missense change affects SMPD1 function (PMID: 19405096). For these reasons, this variant has been classified as Pathogenic. This missense change has been observed in individual(s) with Niemann-Pick A disease and/or Niemann-Pick B disease (PMID: 19405096, 30795770). ClinVar contains an entry for this variant (Variation ID: 2996). This variant is also known as Y467S. This sequence change replaces tyrosine, which is neutral and polar, with serine, which is neutral and polar, at codon 469 of the SMPD1 protein (p.Tyr469Ser). This variant is not present in population databases (gnomAD no frequency). |
Baylor Genetics | RCV000003131 | SCV005052853 | likely pathogenic | Niemann-Pick disease, type A | 2023-12-28 | criteria provided, single submitter | clinical testing | |
OMIM | RCV000003131 | SCV000023289 | pathogenic | Niemann-Pick disease, type A | 2009-07-01 | no assertion criteria provided | literature only |