Total submissions: 4
Submitter | RCV | SCV | Clinical significance | Condition | Last evaluated | Review status | Method | Comment |
---|---|---|---|---|---|---|---|---|
Counsyl | RCV000664760 | SCV000788770 | likely pathogenic | Niemann-Pick disease, type A | 2016-12-29 | criteria provided, single submitter | clinical testing | |
Labcorp Genetics |
RCV001386465 | SCV001586695 | pathogenic | Niemann-Pick disease, type B; Niemann-Pick disease, type A | 2023-08-04 | criteria provided, single submitter | clinical testing | For these reasons, this variant has been classified as Pathogenic. ClinVar contains an entry for this variant (Variation ID: 550117). This variant has not been reported in the literature in individuals affected with SMPD1-related conditions. This variant is not present in population databases (gnomAD no frequency). This sequence change creates a premature translational stop signal (p.Gln10*) in the SMPD1 gene. It is expected to result in an absent or disrupted protein product. Loss-of-function variants in SMPD1 are known to be pathogenic (PMID: 12369017, 15221801). |
Baylor Genetics | RCV000664760 | SCV004205516 | likely pathogenic | Niemann-Pick disease, type A | 2024-01-03 | criteria provided, single submitter | clinical testing | |
Prevention |
RCV003980292 | SCV004788251 | likely pathogenic | SMPD1-related disorder | 2023-11-02 | no assertion criteria provided | clinical testing | The SMPD1 c.28C>T variant is predicted to result in premature protein termination (p.Gln10*). This variant was reported in an individual with Niemann-Pick disease (Vélez Pinos et al. 2023. PubMed ID: 36779112). This variant has not been reported in a large population database (http://gnomad.broadinstitute.org), indicating this variant is rare. Nonsense variants in SMPD1 are expected to be pathogenic. This variant is interpreted as likely pathogenic. |